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Tremblay, J. P., Xiao, X., Aartsma-Rus, A., Barbas, C., Blau, H. M., Bogdanove, A. J., ... Gao, G. (2013). Translating the genomics revolution: the need for an international gene therapy consortium for monogenic diseases. Molecular Therapy, 21(2), p. 266-268.